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Phenylbutyric Acid Modulates Apoptosis and ER Stress-Related Gene Expression in Glycogen Storage Disease Type Ib in Vitro Model

Marina Parezanovic,Nina Stevanovic, Marina Andjelkovic,Milena Ugrin, Sonja Pavlovic,Maja Stojiljkovic,Anita Skakic

MOLECULAR GENETICS & GENOMIC MEDICINE(2025)

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4-PBA,apoptosis,CRISPR/Cas9,ER stress,GSD Ib in vitro model system
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