CRISPR/Cas9 Gene-Edited Hematopoietic Stem Cell Therapy for Sickle Cell Disease
Vionnie W. C. Yu,Yi Liu,Matthew Curran,Pu Zhang,Jennifer Snead,Christian Schmedt,Yi Yang,Victor Guosheng Lin,William R. Tschantz,Lisa Quinn,Carsten Russ,Scott Clarkson,Amy Janiak,Morag Stewart, Yanick Mulumba,Reynald Lescarbeau, Brad Murray,Jessica Seitzer,Walter Strapps,Hon-Ren Huang, Kevin Sloan,Craig S. Mickanin,Lloyd Klickstein,Susan Stevenson BLOOD(2017)
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