Prion Protein Lowering is a Disease-Modifying Therapy Across Prion Disease Stages, Strains, and Endpoints
Eric Vallabh Minikel,Hien T. Zhao,Jason Le,Jill O'Moore,Rose Pitstick,Samantha Graffam,George A. Carlson,Michael P. Kavanaugh,Jasna Kriz,Jae Beom Kim,Jiyan Ma,Holger Wille,Judd Aiken,Deborah McKenzie,Katsumi Doh-Ura,Matthew Beck,Rhonda O'Keefe,Jacquelyn Stathopoulos,Tyler Caron,Stuart L. Schreiber,Jeffrey B. Carroll,Holly B. Kordasiewicz,Deborah E. Cabin,Sonia M. Vallabh Nucleic Acids Research(2020)
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Cellular Prion Protein
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