Functionalized Lipid Nanoparticles for Subcutaneous Administration of Mrna to Achieve Systemic Exposures of a Therapeutic Protein.
Nigel Davies,Daniel Hovdal,Nicholas Edmunds,Peter Nordberg,Anders Dahlen,Aleksandra Dabkowska,Marianna Yanez Arteta,Aurel Radulescu,Tomas Kjellman,Andreas Hoijer,Frank Seeliger, Elin Holmedal, Elisabeth Andihn,Nils Bergenhem,Ann Sofie Sandinge,Camilla Johansson,Leif Hultin,Marie Johansson,Johnny Lindqvist,,Yujia Jing,Stefano Bartesaghi,Lennart Lindfors,Shalini Andersson Molecular Therapy — Nucleic Acids(2021)
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LNP,mRNA,subcutaneous delivery,FGF21,steroid prodrug,tolerability
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