Gene Therapy For Duchenne Muscular Dystrophy Due To Duplications Of Exon 2 Using The Scaav9.U7-Acca Vector: 6-12 Months Clinical Follow UpMegan Ann Waldrop,Michael Lawlor,Tatyana Vetter,Emma Frair,Margaret J. Beatka,Hui Meng,Megan Iammarino,Brenna Powers,Johan Harris,Maryann Kaler,Tabatha Simmons,Kim Mcbride,Nicolas Wein,Kevin FlaniganMOLECULAR THERAPY(2021)引用 1|浏览27AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要