Switching to Glycerol Phenylbutyrate in 48 Patients with Urea Cycle Disorders: Clinical Experience in Spain
Elena Martin-Hernandez,Pilar Quijada-Fraile,Patricia Correcher,Silvia Meavilla,Paula Sanchez-Pintos,Javier de las Heras Montero,Javier Blasco-Alonso, Lucy Dougherty, Ana Marquez,Luis Pena-Quintana,Elvira Canedo,Maria Concepcion Garcia-Jimenez,Pedro Juan Moreno Lozano,Mercedes Murray Hurtado,Maria Camprodon Gomez, Delia Barrio-Carreras,Mariela de los Santos,Mireia del Toro,Maria L. Couce,Isidro Vitoria Minana,Montserrat Morales Conejo,Marcello Bellusci Journal of Clinical Medicine(2022)
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clinical practice,glycerol phenylbutyrate (GPB),sodium benzoate (NaBZ),sodium phenylbutyrate (NaPB),urea cycle disorders (UCDs)
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