Midbrain Gene Therapy for AADC Deficiency
Krystof Bankiewicz,Toni Pearson, Malgorzata Kohutnicka,Waldy San Sebastian,Dora Steel,Robert Spaull,Audrey Soo,Simon Heales,Roser Pons,Angeles Garcia-Cazorla,Salvador Ibanez-Mico,Jolanta Sykut-Cegielska,Krystyna Szymanska,Thomas Opladen,Kathrin Jeltsch,Mari Oppeboen,Herve Testard,Anne Roscher,Sandy Siegert,Michel Willemsen,Saadet Andrews, Bruria Ben-Zeev,Manju Kurian,Miroslaw Zabek MOLECULAR THERAPY(2023)
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