Gene Therapy for Adenosine Deaminase Deficiency: Long-Term Outcome and Post-Marketing Experience
Maddalena Migliavacca,Federica Barzaghi,Claudia Fossati,Paola M. V. Rancoita,Michela Gabaldo,Francesca Dionisio,Stefania Giannelli,Federica Andrea Salerio,Francesca Ferrua,Francesca Tucci,Valeria Calbi,Vera Gallo,Salvatore Recupero,Giulia Consiglieri,Daniela Cesana,Eugenio Montini,Roberta Pajno,Ilaria Monti,Paolo Silvani,Silvia Darin,Miriam Casiraghi,Ambra Corti,Stefano Zancan, Margherita Levi,Dalia AbdElaziz,Ulrich Baumann,Andrea Finocchi,Caterina Cancrini,Saverio Ladogana,Andrea Meinhardt,Isabelle Meyts,Davide Montin,Lucia Dora Notarangelo,Fulvio Porta, Marlene Pasquet,Carsten Speckmann,Polina Stepensky,Alberto Tommasini,Marco Rabusin,Zeynep Karakas,Miguel Galicchio,Lucia Leonardi,Marzia Duse,Sukru Nail Guner,Clelia Di Serio,Fabio Ciceri,Maria Ester Bernardo,Alessandro Aiuti,Maria Pia Cicalese MOLECULAR THERAPY(2023)
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