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Prelimininary Data on Safety and Efficacy of Risdiplam Treatment in a Small Cohort of Adult 5q Spinal Muscular Atrophy

A. Nanni,G. Milella,G. Piccirilli, M. Ucci, S. Idrissi,A. Fraddosio,A. Introna, V. Scacco, M. Megna,I. Simone,E. D'Errico

EUROPEAN JOURNAL OF NEUROLOGY(2023)

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