Real Life Data: Follow-Up Assessment on Spanish Gaucher Disease Patients Treated with Eliglustat. TRAZELGA Project
Irene Serrano-Gonzalo,Laura López de Frutos, Carlos Lahoz-Gil, Francisco Delgado-Mateos,María Ángeles Fernández-Galán,Montserrat Morales-Conejo, María Victoria Calle-Gordo, Daiana Ibarretxe-Gerediaga,Andrés Madinaveitia-Ochoa, Antonio Albarracin-Arraigosa, José Balanzat-Muñoz,Patricia Correcher-Medina,Luis Javier García-Frade,Jesús María Hernández-Rivas, Francesca Labbadia,Jesus Miguel López-Dupla, María Luisa Lozano-Almela,Elvira Mora-Casterá,María Soledad Noya-Pereira, María Ángeles Ruíz-Guinaldo, María del Mar Tormo-Díaz,Isidro Vitoria-Miñana,Isidro Arévalo-Vargas,Marcio Andrade-Campos,Pilar Giraldo Orphanet Journal of Rare Diseases(2023)
Key words
Type 1 Gaucher disease,Biomarkers,Glucosylsphingosine,Lipocalin-2,YKL-40,SF-36,Eliglustat
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