Effect of Nusinersen after 3 Years of Treatment in 57 Young Children with SMA in Terms of SMN2 Copy Number or Type.
Frederique Audic, Sonia M. Dubois,Julien Durigneux,Christine Barnerias,Arnaud Isapof,Marie-Christine Nougues,Jean-Baptiste Davion,Christian Richelme,Carole Vuillerot, Laure Legoff,Pascal Sabouraud,Claude Cances,Vincent Laugel,Juliette Ropars,Caroline Espil-Taris,Valerie Trommsdorff,Anne Perville,Marta Gomez Garcia-de-la-Banda,Herve Testard,Mondher Chouchane,Ulrike Walther-Louvier, Cyril Schweizer,Cecile Halbert, Myriam Badri,Susana Quijano-Roy,Brigitte Chabrol,Isabelle Desguerre ARCHIVES DE PEDIATRIE（2024）
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Spinal muscular atrophy,Nusinersen,SMN2
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