Platform Trial Design for Neurofibromatosis Type 1, NF2-related Schwannomatosis and Non-Nf2-related Schwannomatosis: A Potential Model for Rare Diseases Britt A. E. Dhaenens , Guenter Heimann , Annette Bakker , Marco Nievo , Rosalie E. Ferner , D. Gareth Evans , Pierre Wolkenstein , Jonas Leubner , Cornelia Potratz , Charlotte Carton , Uchenna Iloeje , George Kirk , Jaishri O. Blakeley , Scott Plotkin , Michael J. Fisher , Aerang Kim , Pablo Hernaiz Driever , Amedeo A. Azizi , Brigitte C. Widemann , Andrea Gross , Tom Parke , Eric Legius , Rianne Oostenbrink NEURO-ONCOLOGY PRACTICE（2024）
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neurofibromatosis, schwannomatosis, clinical trial, platform trial, rare diseases
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