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Long-term Treatment of Hereditary Transthyretin Amyloidosis with Patisiran: Multicentre, Real-World Experience in Italy

Neurological sciences official journal of the Italian Neurological Society and of the Italian Society of Clinical Neurophysiology(2025)

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关键词
Hereditary transthyretin amyloidosis,Real-world,Compassionate use programme,Patisiran
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