Long-term Treatment of Hereditary Transthyretin Amyloidosis with Patisiran: Multicentre, Real-World Experience in Italy
Luca Gentile,Anna Mazzeo,Chiara Briani,Silvia Casagrande,Marcella De Luca,Gian Maria Fabrizi,Christian Gagliardi,Chiara Gemelli,Francesca Forcina,Marina Grandis,Valeria Guglielmino,Giacomo Iabichella,Luca Leonardi,Alessandro Lozza,Fiore Manganelli,Roberta Mussinelli,Filomena My,Giuseppe Occhipinti,Silvia Fenu,Massimo Russo,Angela Romano,Alessandro Salvalaggio,Matteo Tagliapietra,Stefano Tozza,Giovanni Palladini,Laura Obici,Marco Luigetti Neurological sciences official journal of the Italian Neurological Society and of the Italian Society of Clinical Neurophysiology(2025)
关键词
Hereditary transthyretin amyloidosis,Real-world,Compassionate use programme,Patisiran
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