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20 Multi-Year Registry Study of Elapegademase-lvlr Treatment in Patients with Adenosine Deaminase Severe Combined Immunodeficiency (ADA-SCID) Requiring Enzyme Replacement Therapy (ERT)

Clinical Immunology(2024)

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关键词
ADA-SCID,Enzyme replacement therapy,Adenosine deaminase severe combined immunodeficiency,HSCT,Registry,Immunodeficiency
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