Editing of Homologous Globin Genes by Nickase-Deficient Base Editor Mitigates Large Intergenic Deletions in HSPCs
MOLECULAR THERAPY NUCLEIC ACIDS（2024）
Key words
MT: RNA/DNA Editing,base editing,CRISPR-Cas9,gamma globin,hemoglobinopathies,large deletions,multiplexed editing,beta globin,gene editing
AI Read Science
Must-Reading Tree
Example
Generate MRT to find the research sequence of this paper
Chat Paper
Summary is being generated by the instructions you defined