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In Vivo Treatment of a Severe Vascular Disease Via a Bespoke CRISPR-Cas9 Base Editor

R, Sabyasachi Das, Vijai Krishnan,Leillani L Ha, Lauren R Fox,Hannah E Stutzman, Claire E Shamber, Pazhanichamy Kalailingam, Siobhan McCarthy,Christian L Lino Cardenas, Claire E Fong,Takahiko Imai, Sunayana Mitra, Shuqi Yun, Rachael K Wood,Friederike M C Benning, Joseph Lawton, Nahye Kim,Rachel A Silverstein,Joana Ferreira da Silva,Demitri de la Cruz, Rashmi Richa,Rajeev Malhotra,David Y Chung,Luke H Chao,Shengdar Q Tsai,Casey A Maguire,Mark E Lindsay,Benjamin P Kleinstiver,Patricia L Musolino

bioRxiv the preprint server for biology(2024)

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