Haematopoietic Gene Therapy of Non-Conditioned Patients with Fanconi Anaemia-A: Results from Open-Label Phase 1/2 (FANCOLEN-1) and Long-Term Clinical Trials Paula Rio , Josune Zubicaray , Susana Navarro , Eva Galvez , Rebeca Sanchez-Dominguez , Eileen Nicoletti , Elena Sebastian , Michael Rothe , Roser Pujol , Massimo Bogliolo , Philipp John-Neek , Antonella Lucia Bastone , Axel Schambach , Wei Wang , Manfred Schmidt , Lise Larcher , Jose C. Segovia , Rosa M. Yanez , Omaira Alberquilla , Begona Diez , Maria Fernandez-Garcia , Laura Garcia-Garcia , Manuel Ramirez , Anne Galy , Francois Lefrere , Marina Cavazzana , Thierry Leblanc , Nagore Garcia de Andoin , Ricardo Lopez-Almaraz , Albert Catala , Jordi Barquinero , Sandra Rodriguez-Perales , Gayatri Rao , Jordi Surralles , Jean Soulier , Cristina Diaz-de-Heredia , Jonathan D. Schwartz , Julian Sevilla , Juan A. Bueren LANCET(2024)
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