Targeted Base Editing Models Hematopoiesis and Pathophysiology of VEXAS Syndrome
Martina Fiumara,Raffaella Molteni,Corrado Campochiaro,Guido Pacini,Alessandro Tomelleri,Elisa Diral,Angelica Varesi,Alessandra Weber,Davide Stefanoni, Roberta Alfieri,Luca Basso-Ricci,Pamela Quaranta,Luisa Albano,Angelo D'Alessandro, Marco Matucci-Cerinic,Raffaella Di Micco,Alessandro Aiuti,Fabio Ciceri,Ivan Merelli,Lorenzo Dagna,Serena Scala,Simone Cenci,Giulio Cavalli,Luigi Naldini,Samuele Ferrari MOLECULAR THERAPY(2024)
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