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Hypomethylating Agents for Patients with VEXAS Without Myelodysplastic Syndrome: Clinical Outcome and Longitudinal Follow-Up of Vacuolization and UBA1 Clonal Dynamics.

Jose R. Alamo, Lucia Mont-de Torres,Sandra Castano-Diez,Anna Mensa-Vilaro, M. Monica Lopez-Guerra,Ines Zugasti, Johana Diaz,Carlos Jimenez-Vicente, Susana Plaza, Virginia Fabregat,Inaki Ortiz de Landazuri,Jordi Yague,Gerard Espinosa,Raimon Sanmarti,Maria Rozman,Francesca Guijarro,Albert Cortes,Ana Triguero, Aina Cardus, Adriana Cuartas, Marina Cornejo,Jordi Esteve,Juan I. Arostegui, Marina Diaz-Beya

BRITISH JOURNAL OF HAEMATOLOGY(2025)

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Key words
hypomethylating agents,myelodysplastic syndrome,<italic>UBA1</italic> mutation,vacuoles,VEXAS syndrome
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