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LONG-TERM SAFETY AND EFFICACY OF FITUSIRAN PROPHYLAXIS IN A PHASE 1/2 OPEN-LABEL EXTENSION STUDY IN PEOPLE WITH MODERATE OR SEVERE HEMOPHILIA A OR B

Steven W. Pipe, Toshko Lissitchkov,Sarah Mangles, Pencho Georgiev, Erin Feng, Laurel A. Menapace, Salim Kichou,Shauna Andersson,Marek Demissie,Margaret Ragni

AMERICAN JOURNAL OF HEMATOLOGY(2024)

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