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Real-world Evidence of Pegcetacoplan in Patients with Paroxysmal Nocturnal Haemoglobinuria: A Nationwide Italian Study.

Elisabetta Metafuni, Filippo Achille Brioschi,Andrea Patriarca, Claudia Leoni, Giorgia Battipaglia, Daniela Carlino, Annalisa Condorelli, Valeria Di Giacomo, Sarah Marktel, Maria Antonietta Marzilli,Maurizio Miglino, Esther Natalie Oliva, Antonella Sau,Alessandra Ricco, Grazia Sanpaolo, Annarita Trolese,Anna Paola Iori,Simona Sica,Wilma Barcellini,Bruno Fattizzo

British journal of haematology(2025)

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